Title:
ＤＭＤのための複数のエキソンスキッピング組成物
Document Type and Number:
Japanese Patent JP6406782
Kind Code:
B2
Abstract:
Provided are antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping, and methods of use thereof to treat muscular dystrophy.
Inventors:
Peter Sotheny
Lizard call
Lizard call
Application Number:
JP2018084126A
Publication Date:
October 17, 2018
Filing Date:
April 25, 2018
Export Citation:
Assignee:
Saleputa Therapeutics, Incorporated
International Classes:
C12N15/113; A61K31/7088; A61K47/50; A61K48/00; A61P21/04
Domestic Patent References:
| JP2003500418A |
Foreign References:
| WO2004048570A1 | ||||
| WO2006000057A1 |
Attorney, Agent or Firm:
Hidesaku Yamamoto
Natsuki Morishita
Natsuki Morishita