COMPOSITIONS AND METHODS FOR MODULATING FMR1 EXPRESSION

Title:

COMPOSITIONS AND METHODS FOR MODULATING FMR1 EXPRESSION

Document Type and Number:

Japanese Patent JP2022063261

Kind Code:

A

Abstract:

To provide methods and compositions for reactivating a silenced FMR1 gene.SOLUTION: In some aspects, methods described by the disclosure are useful for treating a FMR1-inactivation-associated disorder (e.g., fragile X syndrome).SELECTED DRAWING: Figure 5

Inventors:

MICHAEL R GREEN
FANG MINGGANG
WALTER KOWTONIUK

Application Number:

JP2021173030A

Publication Date:

April 21, 2022

Filing Date:

October 22, 2021

Export Citation:

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Assignee:

UNIV MASSACHUSETTS

International Classes:

A61K45/00; A61K31/167; A61K31/4178; A61K31/437; A61K31/496; A61K31/497; A61K31/506; A61K31/522; A61K31/5377; A61K31/548; A61K31/706; A61K31/7088; A61K31/7105; A61K31/713; A61K38/02; A61K39/395; A61K48/00; A61P15/08; A61P25/00; A61P25/14; A61P25/28; A61P43/00

Attorney, Agent or Firm:

Kiyokazu

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