Title:
筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
Document Type and Number:
Japanese Patent JP7370344
Kind Code:
B2
Abstract:
Antisense oligomers complementary to a selected target site in the human dystrophin gene to induce exon 52 skipping are described.
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Inventors:
Bestwick, Richard K.
Hanson, Gunner Jay.
Passini, Marco E.
Schnell, Frederick Joseph
Hanson, Gunner Jay.
Passini, Marco E.
Schnell, Frederick Joseph
Application Number:
JP2020565430A
Publication Date:
October 27, 2023
Filing Date:
May 23, 2019
Export Citation:
Assignee:
Salepta Therapeutics, Incorporated
International Classes:
C12N15/113; A61K31/7088; A61P21/04
Domestic Patent References:
JP2012506703A | ||||
JP2016516066A |
Attorney, Agent or Firm:
Shusaku Yamamoto
Natsuki Morishita
Natsuki Morishita