Title:
血友病Ａ治療に対する遺伝子療法
Document Type and Number:
Japanese Patent JP7347933
Kind Code:
B2
Abstract:
Compositions and regimens useful in treating hemophilia A are provided. The compositions include recombinant adeno-associated virus (rAAV) with a transthyretin enhancer and promoter driving expression of a human Factor VIII.
Inventors:
One, lili
Wilson, James M
Sid Lane, Jenny Agnes
Wilson, James M
Sid Lane, Jenny Agnes
Application Number:
JP2018554331A
Publication Date:
September 20, 2023
Filing Date:
April 13, 2017
Export Citation:
Assignee:
The Trustees of the University of Pennsylvania
International Classes:
C12N15/864; A61K9/10; A61K35/76; A61K48/00; A61P7/04; C12N7/01
Domestic Patent References:
| JP2016500519A | ||||
| JP2002527493A |
Foreign References:
| US20070243168 |
Other References:
Mol Ther.18(1):118-125,2010年
Mol Ther.16(2):280-289,2008年
Mol Ther.16(2):280-289,2008年
Attorney, Agent or Firm:
Patent Attorney Corporation Odashima Patent Office
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