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Title:
CRISPR/CAS構成成分のための脂質ナノ粒子製剤
Document Type and Number:
Japanese Patent JP7245651
Kind Code:
B2
Abstract:
The invention provides lipid nanoparticle-based compositions and methods useful for delivery of CRISPR/Cas gene editing components.

Inventors:
Morrissey, David V.
Patel, Mikhail, Chandrakant
Finn, Jonathan Dee.
Smith, Amy Madison Rhoden
Shaw, Lucinda Jay.
Dombrovsky, Christian
Shah, Ratchi Radraprasad
Application Number:
JP2018551306A
Publication Date:
March 24, 2023
Filing Date:
March 30, 2017
Export Citation:
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Assignee:
Interior Therapeutics, Incorporated
International Classes:
C12N15/09; A61K9/14; A61K38/46; A61K47/24; A61K47/28; A61K48/00; A61P1/16; A61P43/00; C12N15/11; C12N15/55
Domestic Patent References:
JP2012526134A
Foreign References:
WO2014204726A1
WO2015095351A1
WO2015095346A1
Other References:
Mol Pharm, 2014 Mar 3, vol. 11, no. 5, pp. 1424-1434
Human Gene Therapy, 2016 Nov, vol. 27, no. 11, pp. A131 (P280)
Attorney, Agent or Firm:
Hiroshi Kobayashi
Norio Omori
Sayaka Hirakawa
Yasuhito Suzuki