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Title:
トランスサイレチン(TTR)iRNA組成物を用いてTTR関連疾患を治療または予防するための方法
Document Type and Number:
Japanese Patent JP7058656
Kind Code:
B2
Abstract:
The present invention provides methods for treating or preventing TTR-associated diseases using RNAi agents, e.g., double stranded RNAi agents, that target the transthyretin (TTR) gene.

Inventors:
Amy Chan
John Best
Gabriel Robbie
Fusain Zettattawara
Balun Goel
Application Number:
JP2019531922A
Publication Date:
April 22, 2022
Filing Date:
December 15, 2017
Export Citation:
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Assignee:
ALNYLAM PHARMACEUTICALS, INC.
International Classes:
A61K31/713; A61K47/54; A61P3/04; A61P7/00; A61P9/00; A61P25/00; A61P25/02; A61P43/00
Domestic Patent References:
JP2014534244A
Foreign References:
WO2017023660A1
WO2016028649A1
Attorney, Agent or Firm:
Yamato Kento
Norifumi Tomita
Fumio Inai
Manami Sasakura