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Title:
遺伝子疾患の治療のための方法および組成物
Document Type and Number:
Japanese Patent JP6629917
Kind Code:
B2
Abstract:
Methods and compositions for a genetic disease are provided.

Inventors:
Gregory Jay. Cost
Philip Dee. Gregory
Dmitry Gustin
Michael Sea. Holmes
Jeffrey C. Miller
David Passion
Edward Jay. Reaver
Andreas Like
Fiord Urnov
Leysin
Application Number:
JP2018093930A
Publication Date:
January 15, 2020
Filing Date:
May 15, 2018
Export Citation:
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Assignee:
Sangamo Therapeutics, Incorporated
International Classes:
C12N15/55; A61K35/15; A61K35/18; A61K35/28; A61K35/76; A61K38/47; A61K48/00; A61P7/00; A61P7/06; C12N5/078; C12N5/0789; C12N9/16; C12N15/09
Domestic Patent References:
JP2007501626A
JP2009502170A
Other References:
Blood, 2012, Vol.120, No.15, pp.2945-2953
BMC Blood Disorders, 2012, 12:5, p.1-8
Stem Cells, 2011, 29:1717-1726
Trends Biotechnol. (09-May-2013) vol.31, no.7, p.397-405
Science, 2008, Vol.322, No.5909, pp.1839-1842
Nature, 2009, Vol.460, No.7259, pp.1093-1098
Attorney, Agent or Firm:
Hidesaku Yamamoto
Natsuki Morishita
Takatoshi Iida
Daisuke Ishikawa
Kensaku Yamamoto