Title:
METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF SUBJECT IN NEED THEREOF
Document Type and Number:
Japanese Patent JP2019206578
Kind Code:
A
Abstract:
To provide methods for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof.SOLUTION: The present invention relates to methods for performing antisense oligonucleotide-mediated exon skipping in the retina cells of a subject in need thereof, comprising the step of injecting into the vitreous of the subject an amount of the antisense oligonucleotide.SELECTED DRAWING: None
Inventors:
JEAN-MICHEL ROZET
ISABELLE PERRAULT
XAVIER GERARD
JOSSELINE KAPLAN
ARNOLD MUNNICH
ISABELLE PERRAULT
XAVIER GERARD
JOSSELINE KAPLAN
ARNOLD MUNNICH
Application Number:
JP2019145472A
Publication Date:
December 05, 2019
Filing Date:
August 07, 2019
Export Citation:
Assignee:
INST NATL DE LA SANTE & DE LA RECH MEDICAL
FOND IMAGINE
UNIV PARIS DESCARTES
HOPITAUX PARIS ASSIST PUBLIQUE
FOND IMAGINE
UNIV PARIS DESCARTES
HOPITAUX PARIS ASSIST PUBLIQUE
International Classes:
A61K31/7105; A61K31/711; A61K31/712; A61K31/7125; A61K48/00; A61P25/00; A61P25/28; A61P27/02; A61P43/00
Foreign References:
| WO2012168435A1 | 2012-12-13 | |||
| WO2013036105A1 | 2013-03-14 |
Attorney, Agent or Firm:
Patent business corporation Tsukuni