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Title:
アルファ1-アンチトリプシンのモジュレーター
Document Type and Number:
Japanese Patent JP2023520398
Kind Code:
A
Abstract:
アルファ-1-アンチトリプシン欠乏症(AATD)を治療するためのアルファ-1-アンチトリプシン調節因子としてのピロロ[2,3-F]インダゾール及び2,4,5,10-テトラアザトリシクロ[7.3.0.03,7]ドデカ-1,3(7),5,8,11-ペンタエン誘導体。

Inventors:
Giroud, Simon
Boyd, Michael John
Fimonari, Robert Francis Jr.
Zaki, Mariam
Gray, Ronald Lee Jr.
Shoe, Jinwan
Kesaban, Sarati
Nuhunt, Philip Marcel
Garcia Barrantes, Pedro Manuel
Jones, Peter
Brodney, Michael Aaron
Voucher, Diane Marie
Fanning, Rev T.D.
Hall, Amy B.
Harley, Dennis James
Johnson, Mac Arthur Jr.
Maxwell, John Patrick
Sweatshirts, Rebecca Jane
Tapley, Timothy Lewis
Thomson, Stephen A.
Damagnes, Veronique
Cottrell, Kevin Michael
Application Number:
JP2022559584A
Publication Date:
May 17, 2023
Filing Date:
April 02, 2021
Export Citation:
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Assignee:
VERTEX PHARMACEUTICALS INCORPORATED
International Classes:
C07D471/14; A61K31/4162; A61K31/437; A61K31/7056; A61P1/00; A61P1/14; A61P1/16; A61P3/00; A61P11/00; A61P17/00; A61P43/00; C07D487/04; C07H15/26
Attorney, Agent or Firm:
Shusaku Yamamoto
Natsuki Morishita
Takatoshi Iida
Daisuke Ishikawa
Kensaku Yamamoto