Title:
ARTIFICIAL REGULATORY CASSETTES FOR MUSCLE-SPECIFIC GENE EXPRESSION
Document Type and Number:
WIPO Patent Application WO/2022/216988
Kind Code:
A9
Abstract:
A library of artificial muscle-specific expression cassettes (MSECs) for muscle-specific gene expression is described. Different members of the library can be selected for varied transcription levels in different muscle cell types, for different research or therapeutic purposes. MSECs within the library can be used to develop treatments for muscle-related disorders.
Inventors:
CHAMBERLAIN JEFFREY S (US)
HAUSCHKA STEPHEN D (US)
HAUSCHKA STEPHEN D (US)
Application Number:
PCT/US2022/023915
Publication Date:
March 16, 2023
Filing Date:
April 07, 2022
Export Citation:
Assignee:
UNIV WASHINGTON (US)
International Classes:
A61P21/00; C12N15/66; C12N15/67; C12N15/85; C12N15/861
Attorney, Agent or Firm:
WINGER, C. Rachal et al. (US)
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