Login| Sign Up| Help| Contact|

Patent Searching and Data


Title:
COMPOUNDS AND METHODS FOR MODULATION OF SMN2
Document Type and Number:
WIPO Patent Application WO/2018/014041
Kind Code:
A3
Abstract:
Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of spinal muscular atrophy.

Inventors:
RIGO FRANK (US)
PRAKASH THAZHA (US)
SETH PUNIT (US)
Application Number:
PCT/US2017/042463
Publication Date:
April 18, 2019
Filing Date:
July 17, 2017
Export Citation:
Click for automatic bibliography generation   Help
Assignee:
IONIS PHARMACEUTICALS INC (US)
International Classes:
C12N15/113
Foreign References:
US20130289092A12013-10-31
US20160068845A12016-03-10
Other References:
See also references of EP 3484524A4
Attorney, Agent or Firm:
EVANS, William M. et al. (US)
Download PDF:
View/Download PDF      PDF Help



 
Previous Patent: HOLOGRAPHIC SUPERIMPOSITION OF REAL WORLD PLENOPTIC OPACITY MODULATION THROUGH TRANSPARENT WAVEGUIDE...

Next Patent: COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIN TRANSCRIPT