Title:
乳酸デヒドロゲナーゼ（ＬＤＨＡ）遺伝子編集のための組成物及び方法
Document Type and Number:
Japanese Patent JP2022502055
Kind Code:
A
Abstract:
ＬＤＨＡ遺伝子内での、例えば二本鎖切断の導入である、編集のための組成物及び方法を提供する。高シュウ酸尿症を患う対象を治療するための組成物及び方法を提供する。【選択図】図２
Inventors:
Dimek, The Charlie William
Odate, Shob
Huebner, Annette
Cedar, Sri Jani
Murray, Bradley Andrew
Straps, Walter
Odate, Shob
Huebner, Annette
Cedar, Sri Jani
Murray, Bradley Andrew
Straps, Walter
Application Number:
JP2021517350A
Publication Date:
January 11, 2022
Filing Date:
September 27, 2019
Export Citation:
Assignee:
Interior Therapeutics, Incorporated
International Classes:
C12N15/09; A61K31/7105; A61K48/00; A61P3/00; A61P13/02
Attorney, Agent or Firm:
Hiroshi Kobayashi
Junko Kobayashi
Norio Omori
Wataru Ueda
Yasuhito Suzuki
Junko Kobayashi
Norio Omori
Wataru Ueda
Yasuhito Suzuki
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