Title:
COMPOUNDS FOR NONSENSE SUPPRESSION, AND METHODS FOR THEIR USE
Document Type and Number:
WIPO Patent Application WO2006044505
Kind Code:
A3
Abstract:
The present invention relates to methods, compounds, and compositions for treating or preventing diseases associated with nonsense mutations in an mRNA by administering the compounds or compositions of the present invention. More particularly, the present invention relates to methods, compounds, and compositions for suppressing premature translation termination associated with a nonsense mutation in an mRNA.
Inventors:
ALMSTEAD NEIL (US)
KARP GARY M (US)
WILDE RICHARD (US)
WELCH ELLEN (US)
REN HONGYU (US)
KARP GARY M (US)
WILDE RICHARD (US)
WELCH ELLEN (US)
REN HONGYU (US)
Application Number:
PCT/US2005/036764
Publication Date:
July 06, 2006
Filing Date:
October 13, 2005
Export Citation:
Assignee:
PTC THERAPEUTICS INC (US)
ALMSTEAD NEIL (US)
KARP GARY M (US)
WILDE RICHARD (US)
WELCH ELLEN (US)
REN HONGYU (US)
ALMSTEAD NEIL (US)
KARP GARY M (US)
WILDE RICHARD (US)
WELCH ELLEN (US)
REN HONGYU (US)
International Classes:
A61K31/44; A61K31/495; A61K31/53
Domestic Patent References:
| WO2003016280A1 | 2003-02-27 | |||
| WO2004074244A2 | 2004-09-02 |
Download PDF: