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Title:
ホモシスチン尿症の治療する組成物および方法
Document Type and Number:
Japanese Patent JP7009364
Kind Code:
B2
Abstract:
Provided are compositions and methods for enzyme replacement therapy using modified human cystathionine beta synthase (CBS) in the treatment or homocystinuria and related diseases and disorders.

Inventors:
Claus, Jahn Pee.
Maitan, Thomas
Bubrill, Elez
Application Number:
JP2018523444A
Publication Date:
February 10, 2022
Filing Date:
November 09, 2016
Export Citation:
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Assignee:
THE REGENTS OF THE UNIVERSITY OF COLORADO,a body corporate
International Classes:
A61K38/51; A61K31/205; A61K47/60; A61P1/16; A61P13/02; A61P17/14; A61P19/10; A61P27/02; A61P43/00
Foreign References:
WO2014120770A1
Other References:
J. Inherit. Metab. Dis.,2015年08月01日,Vol.39,pp.39-46
Attorney, Agent or Firm:
Makoto Onda
Hironobu Onda
Atsushi Honda
Nakamura Miki



 
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