Title:
COMPOSITIONS AND METHODS FOR MODIFYING A HUMAN DYSTROPHIN GENE
Document Type and Number:
WIPO Patent Application WO/2023/205773
Kind Code:
A3
Abstract:
Provided herein are compositions, systems, and methods comprising effector proteins and uses thereof. These effector proteins may be characterized as CRISPR-associated (Cas) proteins. Various compositions, systems, and methods of the present disclosure may leverage the activities of these effector proteins for the modification, detection, and engineering of nucleic acids.
Inventors:
HARRINGTON LUCAS BENJAMIN (US)
HARTONO WIPUTRA JAYA (US)
LIU PEI-QI (US)
LO DARREN BO YEE (US)
SPER RENAN B (US)
HARTONO WIPUTRA JAYA (US)
LIU PEI-QI (US)
LO DARREN BO YEE (US)
SPER RENAN B (US)
Application Number:
PCT/US2023/066060
Publication Date:
November 30, 2023
Filing Date:
April 21, 2023
Export Citation:
Assignee:
MAMMOTH BIOSCIENCES INC (US)
International Classes:
C12N15/113; C12N9/22; A61K48/00; A61P21/00
Foreign References:
| US20220072537A1 | 2022-03-10 |
Other References:
DATABASE UNIPROTKB ANONYMOUS : "A0A3A9H3W0 ยท A0A3A9H3W0_9FIRM", XP093116024, retrieved from UNIPROT
Attorney, Agent or Firm:
ANTALA, Sagar L. et al. (US)
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