Title:
アンチセンスオリゴヌクレオチド介在性エクソンスキッピングを、それを必要とする対象の網膜において行うための方法
Document Type and Number:
Japanese Patent JP7342047
Kind Code:
B2
Abstract:
The present invention relates to methods for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof. In particular, the present invention relates to a method for performing antisense oligonucleotide-mediated exon skipping in a retina cell of a subject comprising the step of injecting into the vitreous of the subject an amount of the antisense oligonucleotide.
Inventors:
Rose, Jean-Michel
Perot, isabelle
Gerard, Xavier
Kaplan, Josline
Muni, Arnold
Perot, isabelle
Gerard, Xavier
Kaplan, Josline
Muni, Arnold
Application Number:
JP2021006996A
Publication Date:
September 11, 2023
Filing Date:
January 20, 2021
Export Citation:
Assignee:
Ansitu National de la Sant'E de la Cherche Medical
International Classes:
A61K31/7105; A61K31/711; A61K31/7125; A61P27/02
Domestic Patent References:
| JP2019206578A |
Foreign References:
| WO2013036105A1 |
Other References:
臨床薬理,2006年,第37巻 Supplement,S136 IP-009
Attorney, Agent or Firm:
Patent Attorney Corporation Tsukuni
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