TREATMENT OF POMPE'S DISEASE

Title:

TREATMENT OF POMPE'S DISEASE

Document Type and Number:

Japanese Patent JP2017066160

Kind Code:

A

Abstract:

PROBLEM TO BE SOLVED: To provide a method for treatment of Pompe's disease.SOLUTION: The present invention provides a method for treating Pompe's disease using human acid α-glucosidase. According to the present invention, a preferred treatment regime comprises administering greater than 10 mg/kg body weight per week to a patient. The administration is preferably intravenous administration. The method can be used for the treatment of patients with infantile, juvenile or adult Pompe's disease. The human acid alpha glucosidase is preferably obtained in the milk of a nonhuman transgenic mammal, and is preferably predominantly in a 110 kD form.SELECTED DRAWING: None

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Inventors:

VAN BREE JOHANNES BRENARDUS MATHIAS MARIE
VENNEKER EDNA HENRIETTE GERMAINE
MEEKER DAVID P

Application Number:

JP2017000155A

Publication Date:

April 06, 2017

Filing Date:

January 04, 2017

Export Citation:

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Assignee:

GENZYME CORP

International Classes:

A61K38/46; A01K67/027; A61K9/08; A61K9/19; A61K35/20; A61K38/47; A61K47/04; A61K47/10; A61K47/18; A61K47/26; A61K47/42; A61P3/00; A61P3/08; A61P9/04; A61P11/00; A61P43/00; C12N9/24; C12N9/26; C12N15/09; C12N15/85; C12Q1/34; A61K38/00

Attorney, Agent or Firm:

Hidesaku Yamamoto
Natsuki Morishita

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